UCSF researchers hope to cure sickle cell disease through CRISPR gene editing

UCSF researchers hope to cure sickle cell disease through CRISPR gene editing - Blog

With a $17 million grant, UCSF Benioff Children’s Hospital in Oakland will launch a four-year trial evaluating CRISPR/Cas9 gene editing as a potential cure for sickle cell disease. The trial is the first to evaluate the use of non-viral CRISPR gene editing tools to correct a harmful mutation in the beta-globin gene in a patient’s […]