Novel gene editing cell therapy shows curative potential in sickle cell disease

Novel gene editing cell therapy shows curative potential in sickle cell disease - Blog

An experimental gene-editing cell therapy for sickle cell disease has shown encouraging initial results in a multicenter Phase 1 and Phase 2 clinical trial. The clinical trial is the first in which CRISPR-Cas12 is used to edit human cells. Cas12 has been shown in preclinical research to be more effective for gene editing as it […]